Lomitapide in paediatric patients with homozygous familial h…

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  • DOI 10.1016/j.athplu.2025.10.016
  • OpenAlex ID W7117130172
  • Type Article
  • Language EN
  • Published 01 Dec 2025
  • Volume 62
  • Pages 9
  • Source Atherosclerosis Plus
  • Publisher Elsevier BV
  • Countries 9
  • Institutions 24
  • Added 24 Dec 2025
  • Updated 27 Oct 2026
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Lomitapide in paediatric patients with homozygous familial hypercholesterolaemia (HoFH) – Analysis of long-term (104-week) safety and efficacy from the APH-19 study

Article 2025 EN Gold

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UN Sustainable Development Goals
1 SDGs
Authors & Affiliations
17 authors
#AuthorInstitutionsORCID
1 Phil Dawson Chiesi (United Kingdom) (GB) —
2 L. Masana Hospital Universitari Sant Joa… (ES) Universitat Rovira i Virgili (ES)
3 Alberto Zambon University of Padua (IT) MultiMedica (IT)
4 Claus Peter Schmitt University Hospital Heidelberg (DE)
5 Christina Taylan University Hospital Cologne (DE)
6 Joenna Driemeyer University Medical Center Hamb… (DE) —
7 Hofit Cohen Sheba Medical Center (IL) —
8 Paola Sabrina Buonuomo Bambino Gesù Children's Hospit… (IT)
9 Abdullah A. Al-Ashwal King Faisal Specialist Hospita… (SA) —
10 Mohammed Al-Dubayee King Saud bin Abdulaziz Univer… (SA) King Abdullah International Me… (SA)
11 Naji Kholaif Alfaisal University (SA) King Faisal Specialist Hospita… (SA)
12 José Luis Diaz-Diaz Universidade da Coruña (ES) Complexo Hospitalario Universi… (ES) —
13 Faouzi Maatouk Hospital Fatuma Bourguiba Mona… (TN) —
14 Sergio Martínez‐Hervás Universitat de València (ES) Instituto de Salud Carlos III (ES) +3
15 Brian Mangal — —
16 Sandra Löwe Royal Dublin Society (IE) —
17 Zsuzsanna Tamás Chiesi (France) (FR) —

Data: OpenAlex